We have identified a few small molecules (i.e., drugs) that can potentially delay the progression of Wolfram syndrome. Our current focus is to make sure these drugs are safe. Ultimately, we need to confirm the safety in patients by conducting dose escalation studies.
I had productive discussions yesterday. Both meetings were fruitful. I feel hopeful today. Thank you so much for your support and encouragement.
Warmly,
Fumi Urano
