Combating Wolfram Syndrome

There is an urgent need to develop therapeutics for Wolfram syndrome. We need to swiftly test the safety of each new treatment and bring it ...

My team is pursuing multiple therapeutic modalities, including therapies using FDA-approved drugs (drug repurposing), combination therapies,...

My team's new initiative is to develop a "combination therapy" for Wolfram and Type 1 diabetes. What is a "combination th...

Wolfram syndrome is characterized by juvenile-onset diabetes and optic nerve atrophy. Many patients experience diabetes insipidus, hearing i...

I receive many emails and phone calls from patients with genetic disorders, including Wolfram syndrome, and diabetes. Most of them have ques...